Healx
Pipeline
We’re committed to delivering novel treatments to rare disease patients
Program
Indication
AI Discovery
Preclinical
IND enabling
Phase 1
Phase 2
Pivotal (2b/3)
Rare oncology
HLX-1502
Neurofibromatosis Type 1: plexiform/ cutaneous neurofibroma
Neurofibromatosis Type 2
HLX-0213
Neurofibromatosis Type 1
Rare renal
HLX-1066
Autosomal Dominant Polycystic Kidney Disease
HLX-2607
Autosomal Dominant Polycystic Kidney Disease
Rare neurology
HLX-0553
Angelman Syndrome
HLX-0205 + HLX-0206
Fragile X Syndrome
