Pipeline
We’re committed to delivering novel treatments to rare disease patients
Program
Indication
AI Discovery
Preclinical
IND enabling
Phase 1
Phase 2
Pivotal (2b/3)
HLX-1502
Neurofibromatosis Type 1
HLX-0213
Neurofibromatosis Type 1
Undisclosed
Rare and Pediatric Oncology
Rare Neurology
HLX-0206
Fragile X Syndrome
HLX-0553
Angelman Syndrome
Undisclosed
Undisclosed
Rare Renal
HLX-2607
Autosomal Dominant Polycystic Kidney Disease